Emil Kakkis, President of the Kakkis Every Life Foundation, presented at last year's World Orphan Drug Congress USA on the topic â€˜Next steps in accelerating biotechnology for rare diseases.'
Do you want to learn more about:
- Improving access to the accelerated approval pathway thru science-driven regulatory reform
- Helping patients get earlier access to specific, effective treatment
- Developing appropriate surrogate markers
- Driving investment in early stage biotech companies
If so, you need to check out the video below.
For more information on orphan drugs and rare diseases, check out the World Orphan Drug Congress USA. Remember, the earlier you book, the more you save, so register now to secure your seat!