Mary Nathan, a rare disease patient living with Gaucher disease, presented at last year's World Orphan Drug Congress USA on the topic âWhat life has been like with Gaucher disease.'
Do you want to learn more about:
- How enzyme replacement therapy improved her health picture and allowed her to have a surgery that got her out of a wheelchair after seven years
- The special relationship between rare disease patients and the companies that provide drugs and devices to them
If so, you need to check out the video below:
For more information on orphan drugs and rare diseases, check out the World Orphan Drug Congress USA. Remember, the earlier you book, the more you save, so register now to secure your seat!