Rising costs may not be a result of orphan drugs

Published Online: Sep 12,2016 Laurie Toich, Assistant Editor From Daraprim’s price rising 5556% by Turing Pharmaceuticals under the leadership of Martin Shkreli, to the most recent pricing scandal with Mylan’s EpiPen, Americans have been faced with high out-of-pocket costs for many prescription drugs. Government institutions, such as the US Centers for Medicare and Medicaid, have begun crafting novel ways to reduce …

The Netherlands: In the midst of change

  At the World Pharma Pricing & Market Access Congress 2014 conference, Dr Martin van der Graaff, Secretary, Reimbursement Committee, CVZ gave the presentation: “The Netherlands: In the mi(d)st of change” Download and learn: Organisational change in CVZ End of an era: Policy rules and outcomes research First results and experiences with CED Preliminary criteria for prioritizing inpatient drugs Priorities Are …

Obama, Shire, Abbvie

Days After AbbVie-Shire Deal, Obama Slams Tax Inverters

AbbVie recently announced intentions to acquire Shire Pharmaceuticals, and shifting their HQ to Ireland. Obama had some strong words about the practice, known as “Tax Inversion.” When a company acquires another that has business in Ireland, it is possible for that company to shift their HQ from the United States to their newly acquired assets across the Atlantic. This comes …

miRNA targets DNA for Regulation

Regulus Gains Orphan Drug Designation for microRNA Treatment

A recent press release by the company Regulus Therapeutics highlights their newest orphan drug RG-012 – a microRNA treatment designed to help patients with Alport Syndrome, a life-threatening genetic kidney disease that impacts the body’s ability to create a specific type of collagen highly expressed in the kidney and essential to normal kidney structure. The release neglects to mention is that this …

Rare Disease Day: 28th February 2014

This Friday (28th February) its Rare Disease Day across the globe. So we thought we would put together some of the best presentations and posts looking at rare diseases and orphan drugs we’ve had over the last few months. And if these posts don’t satisfy your urge to hear more about the orphan drugs and rare disease industry, then why …

Eldest son of actress Audrey Hepburn named as Rare Disease Day Ambassador 2014

Rare Disease Day 2014 is just 3 weeks away and we understand from EURODIS – the voice of rare disease patients in Europe – that Sean Hepburn Ferrer has been named the Rare Disease Day Ambassador 2014. For the full article, read http://www.rarediseaseday.org/article/sean-hepburn-ferrer-rare-disease-day-2014-ambassador Sean Hepburn Ferrer is the eldest son of the late, beloved Audrey Hepburn, actress and dedicated philanthropist, …