Almost half of cancer patients are diagnosed in late stages

Analysis by Cancer Research UK, released on Monday 22 September, concluded that 46% of cancers in England are diagnosed in the advanced stages. Given the importance of early diagnosis, this would indicates that almost half of cancer patients are diagnosed at a point when treatment will no longer be truly effective. The report, conducted by Incisive Health for CRUK, indicated …

The World Orphan Drug Congress USA is where the rare disease industry comes together to network, learn from each other, and discuss the latest orphan drug developments.

Pat Furlong of Parents Project Muscular Dystrophy on the World Orphan Drug Congress USA

One of the advocacy leaders in the rare disease community is Pat Furlong, President of Parents Project Muscular Dystrophy (PPMD). This April, Ms Furlong will be speaking at the upcoming World Orphan Drug Congress USA in Washington D.C. In this exclusive interview with Rare Disease Report, Ms Furlong explains why she thinks this is one of the most important rare …

We were glad to have the FDA share their stem cells and regenerative medicine expertise at Stem Cells USA.

The FDA on regulatory developments in stem cell, cell and gene therapies

Mohammad Heidaran, of the Office of Cellular, Tissue and Gene Therapies, CBER at the FDA, presented at the Stem Cells & Regenerative Medicine Congress in 2013. Enclosed are his presentation slides from the event, where he addresses clarifying aspects like potency assays, purity and identity assessment. You can now view the recording of his presentation alongside these slides, so that …

AstraZeneca and Bristol-Myers Squibb Diabetes Alliance Provides $5 Million Grant for American Diabetes Association’s Pathway to Stop Diabetes Research Initiative

With diabetes projecting to hit more than half a billion of the population by Year 2035, there is an increasing need to look into diabetes management and personalized treatment. In view of this, AstraZeneca and BMS U.S Diabetes Alliance will be supporting the American Diabetes Association’s Pathway to stop Diabetes research program in a three-year grant.  The objective is to …

Challenges and opportunities in the treatment of rare diseases

Rare diseases affect more than 55 millions patients in US and EU alone, highlighting the huge societal impact of these diseases.  The various clinical, regulatory and commercial challenges to develop treatment for these diseases call for actions from various parties involved.  One of the successful initiatives is the orphan drug legislation by FDA in US.  Prior to the Orphan Drug …

Stem Cells take on chemotherapy side effects

Researchers find a way to use stem cells to fight the side effects of chemotherapy Read the original article here Scientists at the Fred Hutchinson Cancer Research Center have been working on a way to lessen the harmful side effects of chemotherapy. Chemo is used as a therapy to kill cancer cells, but has heavy negative side effects for the …