US-Market-Size-Infographic

Infographic: What is the size of the Orphan Drugs Market in the USA?

Here at World Orphan Drug Congress USA, we understand that sometimes it is really useful to have the stats! So here they are – in a handy infographic! We thought this breakdown and overview might be helpful to some in the orphan drug sector. We took this from the FDA’s list of approved and designated orphan drugs and is one …

Contemporary Science Insights: Next Generation Therapies

In general terms, stem cells are cells that can duplicate themselves and differentiate into cell types found in the body. However stem cells are not all equal. Embryonic stem (ES) cells can transform into any cell type found in the body and this gives rise to the term, “pluripotent” cells. Human ES cells are obtained from pre-implantation embryos, created using in …

The World Orphan Drug Congress USA is where pharma, government, and patient groups gather to network, learn from each other, and discuss the latest orphan drug and rare disease strategies and technologies.

The Role of Specialty Pharmacy in Orphan Drug Therapy

Orsini Healthcare is a leading national specialty pharmacy focused on the delivery of specialty medications to patients with rare conditions. Their disease-specific clinical CareTeam programs, commitment to high-touch customer service, and our patient centered approach ensures satisfaction and adherence to treatment. Orsini Healthcare will be exhibiting at this year’s World Orphan Drug Congress USA, and we were lucky enough to …

Why orphan drugs are a key part of pharma’s future?

Back in the 1980's when the Orphan Drug Act was created, legislators, government agencies and even industry weren't expecting that it would create a multi-billion dollar market where companies now fight fiercely for a share in this segment. It's also understood that the timing of the Act was very fortuitous as it was closely aligned with the beginning of US' …

Acupuncture helpful to COPD patients

COPD patients benefit from acupuncture Read the original article here Researchers in Japan have recently come to the conclusion that will help lend some hope to those suffering from Chronic Obstructive Pulmonary Disease, or COPD. A study conducted on 68 patients with COPD has seemed to demonstrate that acupuncture may help alleviate symptoms of the disease. COPD is a rare …

Kenta Biotech takes on pneumonia

New orphan drug from Kenta Biotech will help fight pneumonia Read the original article here In recent years, health care professionals have been experiencing more and more difficulty effectively treating pneumonia. This is due to the development of drug-resistant strains of the illness. Growing gaps between supply and demand in effective treatment has not helped doctors either. This is why …

Getting high with Multiple Sclerosis patients

Researchers at the University of California find more positive benefits of marijuana Read the original article here Jody Corey-Bloom, MD, PhD of the Multiple Sclerosis Center at the University of California San Diego, is the researcher in charge of a study on the effects of marijuana on sufferers of MS. This study has recently released findings that marijuana has the …

NORD honors advocates of #RareDisease patients

NORD celebrates those who have made a difference in the lives of rare disease patients Read the original article here This Tuesday, May 15, the National Organization for Rare Disorders will hold the awards ceremony for its Partners in Progress Celebration. The ceremony will be held at Union Station in Washington, D.C. NORD will acknowledge those who have made a …